Migalastat

Migalastat

Cat Number
API108147542
CAS Number
108147-54-2

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CAS Number
108147-54-2
Synonyms
1-deoxygalactonojirimycin (2R,3S,4R,5S)-2-(hydroxymethyl)piperidine-3,4,5-triol DDIG
Description
Migalastat is pharmacologic chaperone of alpha-galactosidase the intrahepatic enzyme that is deficient in Fabry disease. Clinical experience with migalastat is limited, but it not been linked to serum enzyme elevations during therapy or to instances of clinically apparent acute liver injury.
Molecular Formula
C6H13NO4
Molecular Weight
163.17
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