Givosiran

Cat Number
PIPB-0191
CAS Number
1639325-43-1

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CAS Number
1639325-43-1
Synonyms
ALN-AS1;21-[(2-Acetamido-2-deoxy-β-D-galactopyranosyl)oxy]-N-[3-({5-[(2-acetamido-2-deoxy-β-D-galactopyranosyl)oxy]pentanoyl}amino)propyl]-6-[(3-{[3-({5-[(2-acetamido-2-deoxy-β-D-galactopyranosyl)oxy ]pentanoyl}amino)propyl]amino}-3-oxopropoxy)methyl]-6-({12-[(2R,4R)-4-hydroxy-2-methyl-1-pyrrolidinyl]-12-oxododecanoyl}amino)-11,17-dioxo-4,8-dioxa-12,16-diazahenicosan-1-amide
Description
Givosiran is a small interfering RNA targeting liver aminolevulinic acid synthase 1(ALAS1) messenger RNA.
Molecular Formula
C78H139N11O30
Molecular Weight
1710.99
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